Home treatment of type VI mucopolysaccharidosis (Maroteaux-Lamy syndrome) an alternative at this time of COVID-19 pandemic: A case in Peru

Cortez Miranda J.L.; Blacido Trujillo L.; Liendo Chocano M.E. · Clinical Case Reports (2020) · DOI: 10.1002/ccr3.3420

Resumen

We report a patient with mucopolysaccharidosis type VI, on long-term enzyme replacement home therapy. Results support the efficacy and safety benefits, with additional advantage of home therapy to minimize the risk of community-transmitted infections.